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Palo Alto Investors LP 13F holdings, Q3 2025

Holdings as of September 30, 2025 · filings on SEC EDGAR · latest filing →

Palo Alto Investors LP disclosed 44 US equity positions worth $540.4m in its Q3 2025 13F filing. The largest position was INSM at 13.1% of the reported book, followed by PTCT and ACAD. Against the Q2 2025 filing, it opened 3 new positions, added to 13 and reduced 19 among the top 44 holdings.

← Q2 2025 · Q4 2025 →

What did Palo Alto Investors LP own in Q3 2025? Top 44 positions

#StockSectorWeightValueSharesΔ sharesvs Q2 2025
1 INSM INSMED INC Healthcare 13.1%$70.8m491,805 -43% reduced
2 PTCT PTC THERAPEUTICS INC Healthcare 9.8%$52.9m862,613 112% added
3 ACAD ACADIA PHARMACEUTICALS INC Healthcare 9.7%$52.6m2,466,684 -4% reduced
4 AM6 AMICUS THERAPEUTICS INC 7.8%$42.3m5,367,798 -4% reduced
5 BMRN BIOMARIN PHARMACEUTICAL INC Healthcare 7.6%$40.8m754,007 -10% reduced
6 BIIB BIOGEN INC Healthcare 4.8%$26.0m185,661 -10% reduced
7 UTHR UNITED THERAPEUTICS CORP Healthcare 4.5%$24.4m58,186 -39% reduced
8 ANAB ANAPTYSBIO INC Healthcare 3.8%$20.6m673,520 -17% reduced
9 IOVA IOVANCE BIOTHERAPEUTICS INC Healthcare 3.1%$16.5m7,618,132 122% added
10 NVCR NOVOCURE LTD Healthcare 3.0%$16.2m1,256,159 31% added
11 DYN DYNE THERAPEUTICS INC Healthcare 3.0%$16.0m1,262,674 377% added
12 IRON DISC MEDICINE INC Healthcare 2.7%$14.8m224,300 54% added
13 ALNY ALNYLAM PHARMACEUTICALS INC Healthcare 2.7%$14.7m32,320 -57% reduced
14 GOSS GOSSAMER BIO INC Healthcare 2.7%$14.4m5,464,349 -5% reduced
15 PROTHENA CORP PLC 2.4%$12.9m1,324,028 4% added
16 RARE ULTRAGENYX PHARMACEUTICAL IN Healthcare 2.1%$11.1m369,531 658% added
17 AGIO AGIOS PHARMACEUTICALS INC Healthcare 2.0%$10.7m265,497 -1% reduced
18 SNDX SYNDAX PHARMACEUTICALS INC Healthcare 1.9%$10.1m654,930 47% added
19 EHTH EHEALTH INC Financial Services 1.2%$6.7m1,544,619 -2% reduced
20 DNLI DENALI THERAPEUTICS INC Healthcare 1.1%$5.9m408,006 70% added
21 ALGN ALIGN TECHNOLOGY INC Healthcare 1.1%$5.7m45,735 21% added
22 ALKS ALKERMES PLC Healthcare 1.0%$5.5m183,938 -17% reduced
23 RNAGBP AVIDITY BIOSCIENCES INC 0.9%$4.8m109,831 -8% reduced
24 MIRM MIRUM PHARMACEUTICALS INC Healthcare 0.9%$4.7m64,700 0% held
25 CDNA CAREDX INC Healthcare 0.9%$4.6m316,204 – new
26 TSHA TAYSHA GENE THERAPIES INC Healthcare 0.8%$4.1m1,246,033 0% held
27 NUVB NUVATION BIO INC Healthcare 0.7%$3.8m1,020,547 32% added
28 ACRS ACLARIS THERAPEUTICS INC Healthcare 0.6%$3.0m1,566,840 13% added
29 CRSP CRISPR THERAPEUTICS AG Healthcare 0.5%$2.7m41,226 -8% reduced
30 TVTX TRAVERE THERAPEUTICS INC Healthcare 0.5%$2.6m110,719 0% held
31 EW EDWARDS LIFESCIENCES CORP Healthcare 0.5%$2.6m33,640 -15% reduced
32 NBIX NEUROCRINE BIOSCIENCES INC Healthcare 0.5%$2.5m18,117 36% added
33 STOK STOKE THERAPEUTICS INC Healthcare 0.5%$2.5m105,427 -16% reduced
34 PYXS PYXIS ONCOLOGY INC 0.4%$2.3m1,037,421 0% held
35 BNTX BIONTECH SE-ADR Healthcare 0.4%$1.9m19,614 -22% reduced
36 BCYC BICYCLE THERAPEUTICS PLC-ADR Healthcare 0.3%$1.7m221,071 -11% reduced
37 ALDX ALDEYRA THERAPEUTICS INC Healthcare 0.2%$1.2m225,465 0% held
38 HUM HUMANA INC Healthcare 0.2%$1.0m3,985 0% held
39 ORKA ORUKA THERAPEUTICS INC Healthcare 0.1%$791.3k59,985 – new
40 ABEO ABEONA THERAPEUTICS INC Healthcare 0.1%$574.8k108,865 0% held
41 URGN UROGEN PHARMA LTD Healthcare 0.1%$488.8k24,500 0% held
42 PROQR THERAPEUTICS NV 0.1%$402.2k188,807 – new
43 AKTX AKARI THERAPEUTICS PLC-ADR 0.0%$147.5k146,024 0% held
44 GBIOGBX GENERATION BIO CO 0.0%$92.1k15,047 -90% reduced

Weights are shares of the reported long US equity book (options excluded). Values are as filed, normalised to whole dollars. Share changes compare against the immediately preceding filing only.